... References Hemophilia — American Society of Gene + Cell Therapy Roctavian Highlights of Prescribing Information — BioMarin Pharmaceutical Inc. ...
... As of October 2025, valoctocogene roxaparvovec (Roctavian) is the only approved gene therapy for hemophilia A. ...
... Etranacogene dezaparvovec-drlb (Hemgenix) is approved to treat hemophilia B, and valoctocogene roxaparvovec-rvox (Roctavian) is approved for severe hemophilia A. ...
8 Facts About Hemophilia You Should Know
... Etranacogene dezaparvovec-drlb (Hemgenix) is approved to treat hemophilia B, and valoctocogene roxaparvovec-rvox (Roctavian) is approved for severe hemophilia A. ...
... With a working copy of the gene, a person with hemophilia may be able to make the missing clotting factor on their own.Valoctocogene roxaparvovec-rvox (Roctavian) is FDA-approved to treat severe hemophilia A. Etranacogene dezaparvovec-drlb (Hemgenix) is a gene therapy approved for hemophilia B. ...
How To Treat Hemophilia: 6 Treatment Options
... With a working copy of the gene, a person with hemophilia may be able to make the missing clotting factor on their own.Valoctocogene roxaparvovec-rvox (Roctavian) is FDA-approved to treat severe hemophilia A. Etranacogene dezaparvovec-drlb (Hemgenix) is a gene therapy approved for hemophilia B. ...